Drug reference
migalastat
Oral chaperone therapy
Oral chaperone therapy
CDSCO approved
EXCRETION
—
not curated
INTERACTIONS
—
none in our sources
PREGNANCY
—
not curated
Mechanism
Stabilizes mutant forms of alpha-galactosidase, increasing its enzymatic activity.
Indications
Fabry's disease (specifically for patients with variants amenable to this therapy)
Related guidelines
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Sources: Harrison 22e·Verified: 2026-05-10 · House clinical team