Drug reference directory
Drug reference

migalastat

Oral chaperone therapy

Oral chaperone therapy
CDSCO approved
EXCRETION
—
not curated
INTERACTIONS
—
none in our sources
PREGNANCY
—
not curated

Mechanism

Stabilizes mutant forms of alpha-galactosidase, increasing its enzymatic activity.

Indications

Fabry's disease (specifically for patients with variants amenable to this therapy)

Drug interactions

1 additional unreviewed or low-confidence interaction hidden because their provenance or source detail is insufficient.

Related guidelines

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Textbook-sourced·Sources: Harrison 22e·Updated: 2026-05-10